Genetic Therapies Focus Group - Post Meeting

Question Title

* 1. Do you feel more educated about gene therapies now?

Yes

No

Yes, but I want to know more

Question Title

* 2. Which gene therapy method is ready to enroll trial participants in the 3rd quarter of 2023?

CRISPR - editing

AAV9 delivered genetic therapy - modification

Question Title

* 3. Do you have a better understanding of why immunosuppression is needed with an AAV9 delivery system?

Yes

No

I don't know what that means

Question Title

* 4. If an ICD was required prior to gene therapy would you be willing to get one or would you prefer to use a wearable life-vest?

I already have an ICD

I would be willing to get an ICD

I would agree to wear a life vest for the duration of the trial (3-6 months)